Pioneering RNA-targeting gene therapies

Addressing human genetic disease by targeting RNA


Mutations in our DNA can cause disease and our RNA-targeting technology platform allows us to precisely  address these mutations. By targeting RNA, our approach avoids the risk of off-target effects in DNA and is suited to address many diseases linked to dysfunctional processing of RNA.  We are focused on realizing the potential of our RNA-targeting gene therapy platform to treat a range of devastating illnesses.


James Burns, PhD

Chief Executive Officer

Ron Batra, PhD

Vice President, R&D

Kathie Bishop, PhD

Chief Scientific Officer

Holly Winter

Vice President, Human Resources

Micah Mackison

Chief Business Officer

Gene Yeo, PhD, MBA

Scientific Advisor




December 10, 2019 - Press Release

Locana Expands Leadership Team with Appointment of former Casebia CEO, James Burns, Ph.D., as Chief Executive Officer

San Diego,  CA -- Locana, Inc., a leading RNA-targeting gene therapy company, today announced...

September 23, 2019 - Press Release

Biocom Announces Fourth Annual Catalyst Award Winners

San Diego,  CA -- Biocom, the association representing the California life science industry, today...

September 4, 2019 - Press Release

Locana Appoints Kathie Bishop, Ph.D., as Chief Scientific Officer

San Diego,  CA -- Locana, a leading RNA-targeting gene therapy company, today announced...

June 12, 2019 - Press Release

MDA Awards Venture Philanthropy Grant to Locana to Develop Novel

Treatment for Muscular Dystrophy

New York, NY and San Diego,  CA -- The Muscular Dystrophy Association (MDA) and Locana, a leading...

May 22, 2019 - Press Release

Locana Raises $55 Million Series A Financing to Advance Portfolio of RNA-targeting Gene Therapies

San Diego, CA -- Locana Raises $55 Million Series A Financing to Advance Portfolio of RNA-targeting...

August 10, 2017 - News Coverage, Fierce Biotech

RNA-targeting CRISPR could yield treatments for Huntington's, ALS

Researchers from the University of California, San Diego, have used a new version of the gene editing...

October 5, 2017 - News Coverage, MIT Technology Review

Arming Bodies with CRISPR to Fight Huntington’s Disease and ALS

The editing tool normally targets DNA, but scientists are aiming it at a different molecule...

August 13, 2017 - News Coverage, Engadget

Gene editing technique could treat ALS and Huntington's disease

It might delay the onset of conditions that are normally inescapable...

December 12, 2016 - News Coverage, Discover

Top 100 Stories of 2016: CRISPR Edits Cells' RNA

It's a first step toward treating diseases like muscular dystrophy and neurodegeneration...

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